Researchers at San Diego State University and Michigan State University are shedding new light on how viruses meticulously ...

Since 2008, the FDA has approved 11 treatments for a rare genetic condition called hereditary angioedema (HAE), three of ...

The collaboration will explore RNA-based small molecule drug candidates aimed at neurological conditions where existing ...

DAWNZERA is the first and only RNA-targeted medicine approved for HAE, designed to target plasma prekallikrein (PKK), a key protein that activates inflammatory mediators associated with acute attacks ...

The approval makes donidalorsen the only treatment in the US for hereditary angioedema that is an RNA-targeted prophylactic.

Sarepta is facing a number of issues currently, including platform-level safety concerns, management credibility issues, etc.

In June, the monoclonal antibody garadacimab (Andembry) was approved for prevention of HAE attacks at a dose of once monthly ...

Single-cell proteomics with RNA sequencing uncover hidden gene expression dynamics in stem cell differentiation.

The quest for a vaccine against HIV has been going on for about 40 years — almost as long as the virus that causes AIDS has ...

The ability to correct disease-causing genetic mistakes using genome editors holds great promise in medicine, but it is not ...

The ability to correct disease-causing genetic mistakes using genome editors holds great promise in medicine, but it is not without risk. When this type of "genetic surgery" is performed on DNA, for ...

In 1957, just four years after Francis Crick and other scientists solved the riddle of DNA’s structure—the now famous double ...