DEER PARK, Ill., Dec. 17, 2024 (GLOBE NEWSWIRE) -- Eton Pharmaceuticals, Inc. (ETON), an innovative pharmaceutical company focused on developing and commercializing treatments for rare diseases ...
A PTC Therapeutics drug in development for an inherited metabolic disorder has achieved the main goal of a pivotal study, results that support bringing the therapy to regulators. But less clear is how ...
- Oral Presentation on In Vivo Gene Therapy Product Candidate and Data on Gene Editing Candidate Paved Way for Initiation of juMPStart and pheEDIT Trials - In the oral presentation titled, “Long-Term ...
Results support advancement to Phase 1b study in individuals with PKU; study now open for enrollment BOSTON, May 31, 2023 (GLOBE NEWSWIRE) -- Jnana Therapeutics, a clinical-stage biotechnology company ...
The results of the preclinical study demonstrate improved muscle anabolism and function with a prolonged-release amino acid supplement using Physiomimic Technology™ GENEVA, SWITZERLAND / ACCESSWIRE / ...
A special diet is the main treatment for phenylketonuria. Medications are also available. Treatment and monitoring is lifelong. Phenylketonuria (PKU) is an inherited condition where the amino acid ...